Patients with spinal muscular atrophy (SMA) type 2 showed improved motor ability when treated with intrathecal onasemnogene ...

Creatinine, a byproduct of muscle function, may be more sensitive in tracking SMA progression and response to treatment than ...

Men with SMA are likely to have fertility issues, and patients with more severe motor impairments have lower sperm counts, ...

Advocates rallied outside the State House on Tuesday for special education funding.The group urged lawmakers to allocate more ...

Accessible travel blog founder Cory Lee is committed to helping other wheelchair users travel the world freely.

Positive results from its Phase III STEER study mean Novartis could boost sales of its OAV101 IT drug for spinal muscular ...

Scholar Rock aims for a 2025 launch of apitegromab in SMA, expecting $2 billion in global revenue and significant growth from upcoming trials and favorable data.

Back to Healio Topline results from a phase 3 clinical trial showed an investigational gene therapy for young people with spinal muscular atrophy type 2 increased mobility and slowed disease ...

Crystal Rondeau’s muscle wasting disease has left her with only one finger to press an alarm button or send a text. The ...

—A new study analyzed health-related quality of life (HRQoL) using 5 generic and neuromuscular disease-specific rating scales in German children with spinal muscular atrophy (SMA), most of whom ...