Health activists demand government action to reduce the cost of SMA medicines, citing constitutional obligations and ...
By clicking “Accept All Cookies”, you agree to the storing of cookies on your device to enhance site navigation, analyze site ...
A man with a muscle-wasting disease is pleased Manitoba is asking a federal agency to reconsider its opposition to a ...
More research is needed to confirm gray matter, the darker tissue found in the brain and spinal cord, “as a potential disease ...
Filmmaker Reid Davenport weaves a powerful first-person perspective with a journalistic investigation about disability ...
Patients with spinal muscular atrophy (SMA) type 2 showed improved motor ability when treated with intrathecal onasemnogene ...
The health activists argue that the government is empowered with effective law and policy tools and therefore should ...
An investigational higher dose of spinal muscular atrophy drug nusinersen gains attention as the FDA and European Medicines ...
Application is supported by results from the DEVOTE study, which suggested that two doses of Spinraza (nusinerse) 50 mg taken ...
SPINRAZA is an approved treatment for spinal muscular atrophy in over 71 countries ... of the higher dose regimen in children and adults who transitioned from SPINRAZA 12 mg to the 50/28 mg ...
We are pleased to announce that our applications for the higher dose regimen of nusinersen are now under review in the US and Europe,” said Stephanie Fradette, Pharm.D., Head of the Neuromuscular ...