The dire circumstances facing cystic fibrosis patients in Cuba have come to light through a heartfelt letter sent to our news ...

modulator for the treatment of cystic fibrosis (CF) in people 6 years and older who have at least one F508del mutation or another mutation in the CFTR gene that is responsive to ALYFTREK.

Cystic fibrosis is a genetic disorder that affects various organs ... Cystic fibrosis transmembrane conductance regulator (CFTR) modulators are a class of medications that help improve the ...

Lung biopsy results demonstrated widespread CFTR transgene RNA and protein ... "4DMT reveals positive interim Phase I/II data for cystic fibrosis gene therapy" was originally created and published ...

Cystic fibrosis is a genetic condition that causes mucus in the body to become thick and sticky. The mucus throughout the body is typically slippery and acts as a protective barrier in the lungs ...

An additional 94 non-F508del CFTR mutations and a boxed warning on liver injury and liver failure were included in the updated prescribing information. 1507_1515del9, 2183A→G, A1067P ...

Lupin Ltd received tentative approval from the USFDA for its generic version of Ivacaftor oral granules, used for treating cystic fibrosis. The product, produced at Lupin's Nagpur facility, may ...

Lupin receives USFDA approval for its generic version of Ivacaftor oral granules, a treatment for cystic fibrosis. The ...

Ivacaftor Oral Granules, 25 mg, 50 mg and 75 mg per unit dose packet are indicated for cystic fibrosis treatment in patients ...

Arcturus Therapeutics initiates patient dosing in phase 2 multiple ascending dose studies for CF and OTC deficiency: San Diego Wednesday, January 8, 2025, 13:00 Hrs [IST] Arcturus ...