[72] The ideal biomarker for gene therapy trials would change quickly ... proof-of-principle for gene transfer into the cystic fibrosis (CF) lung. It is currently unknown whether gene transfer ...
The Massachusetts-based biotech plans to use the funds to push its candidates into mid-stage clinical trials in a space ...
By the time Enid Katz was two years old, she had already suffered through several bouts of bronchitis and was always hungry, ...
The cystic fibrosis transmembrane regulator (CFTR) gene was isolated as the cause of cystic fibrosis (CF) in 1989. By 1993, gene therapy treatments for patients with CF began in earnest. While early ...
Allison John and Rocky When Allison John was 13 and watching the science programme Tomorrow’s World , a segment on gene therapy came up. This was cutting edge stuff in the early 1990s and John had ...
Sionna Therapeutics is eyeing a $156 million IPO as the cystic-fibrosis-focused biotech looks to take its lead candidate into ...
When cystic fibrosis hits your lungs hard, hit back. Everything you need to know about getting your lungs back into shape is ...
Some people with cystic fibrosis still do not have access to the life-changing modulator therapy drugs, despite wider EMA ...
Vertex Pharmaceuticals (NASDAQ:VRTX), a leading biotechnology company known for its cystic fibrosis (CF) treatments, is at a critical juncture as it seeks to diversify its portfolio and maintain its ...
A Wicklow mother is among a concerned group of parents who are calling for individual trials of the modulator therapies for ...