Independent.ie1d
‘Time is precious’ – children with rare cystic fibrosis gene denied access to potentially life-extending therapies
Children whose cystic fibrosis is caused by a rare gene variant are excluded from a new treatment which could potentially ...
'I have that guilt': I'm A Celeb star Reggie Bird opens up about her son's battle with the genetic disorder cystic fibrosis
I’m A Celebrity…Get Me Out Of Here star Reggie Bird has opened up about caring for her son with cystic fibrosis and says she ...
Woman with cystic fibrosis to embark on 3,200 mile row across Atlantic Ocean in historic world-first
Sophie would make a world record for being the first man or woman with cystic fibrosis to row across the Atlantic, while at ...
imt.ie4d
Call for children with cystic fibrosis and rare genes to gain access to life-saving therapy
Some people with cystic fibrosis still do not have access to the life-changing modulator therapy drugs, despite wider EMA ...
Medical Xpress on MSN10d
New animal model offers insights into pancreatic disease and diabetes
Cystic fibrosis (CF) is a life-threatening genetic disease affecting multiple organ systems, with pancreatic dysfunction ...
Is Vertex Pharmaceuticals Stock a Buy in 2025?
The bottom line is few companies can match its combination of established leadership in rare diseases and realistic pathways ...
Irish Independent on MSN1d
Wicklow mother calls for access to life-saving therapy for son with rare form of Cystic Fibrosis
A Wicklow mother is among a concerned group of parents who are calling for individual trials of the modulator therapies for ...
Justin Baldoni’s lawyer previously represented man suing actor over ‘Five Feet Apart’ script
Travis Flores accused Baldoni of copyright infringement and breach of contract over the movie, which he claimed ripped off ...
Devyser Diagnostics AB: Devyser wins tender in Italy for its cystic fibrosis NGS test worth up to 5.4 million SEK
Devyser has secured a tender for its cystic fibrosis NGS test, Devyser CFTR. The tender with Policlinico di Bari is valid for five years with an estimated total order value up to 5.4 million SEK "This ...
Can you get disability benefits for cystic fibrosis? 3 things to do if your claim is denied
If you receive a denial letter from your insurer, don’t appeal the decision before seeking legal advice, says a leading ...