Cystic fibrosis is a genetic disorder that affects various organs, including the lungs and digestive system. Medications are important for managing symptoms, but there is currently no cure for the ...
A novel once-daily drug showed a comparable efficacy and safety profile as the standard-of-care drug in patients with cystic ...
Patients aged 6 to 11 years with cystic fibrosis receiving 24-week once-daily vanzacaftor/tezacaftor/deutivacaftor generally ...
A 26-year-old woman with cystic fibrosis successfully received her third ... But before a match could be found, she was forced to use an oxygen tank and suffered from severe fatigue and loss ...
Cystic fibrosis (CF) is a single-gene disorder with ... Thus, it is not surprising that in the early years of gene therapy, CF was at the forefront of this field. Since cloning of the CF gene ...