Nov. 13, 2024 — The Huntington's disease (HD) mutation eventually causes a fatal brain disease in adulthood, but a new study finds that early in life, children with the HD mutation have bigger ...

A patient in the UK has received a new therapy for Huntington’s disease, which experts hope ... ALN-HTT02 is a type of molecule called a small interfering RNA (siRNA). It is designed to lower ...

While discovering that DNA is itself a long polymer made out of four different types of small ... such is the case in Huntington's disease. Remarkably, the toxic configuration is often able ...

Study finds β-blockers may delay onset and slow progression of Huntington's disease ... s disease. However, the researchers believe that the variability in the effects across different β ...

In a Type B meeting, the FDA signified that it will allow uniQure to use a natural history control, the composite Unified ...