In their 2019 paper, Liu’s team used prime editing to alter the gene mutations causing sickle cell disease ... a lung biologist and research director at Cystic Fibrosis Trust, who was not involved in ...

In January 2023, Asklepios BioPharmaceutical entered a research partnership with ReCode to explore a single-vector gene-editing platform. "ReCode to secure funds for cystic fibrosis gene ...

Viral and nonviral clinical trials have established proof-of-principle for gene transfer into the cystic fibrosis (CF) lung. It is currently unknown whether gene transfer efficiency is sufficient ...

Despite new medication, cystic fibrosis often leads to permanent lung damage. Working with an international team, researchers ...

Cystic fibrosis (CF) is a genetic disorder that ... too expensive to be repeated each time this happens. This is why gene ...

Compare that with a disease like cystic fibrosis, which is caused by more ... creating hundreds or thousands of different gene editing drugs for every single mutation is very impractical, right?” ...

Gene therapy and gene editing are on the cutting ... company that specializes in developing therapies to treat cystic fibrosis. Vertex also owns the rights to 60% of the profits from sales of ...

The Massachusetts-based biotech plans to use the funds to push its candidates into mid-stage clinical trials in a space ...

Cystic fibrosis (CF) is a life-threatening genetic ... The team developed their CF rabbit model using CRISPR/Cas9 gene-editing technology. Rabbits with CF exhibited hallmark pancreatic changes ...

CRISPR is a powerful gene-editing tool that holds enormous potential ... sickle cell anemia, cystic fibrosis, Alzheimer’s, Duchnene muscular dystrophy (DMD), and other chronic musculoskeletal ...