New therapy for Huntington’s disease ‘may slow progression’ - There are thought to be around 7,000 people living with ...
In a Type B meeting, the FDA signified that it will allow uniQure to use a natural history control, the composite Unified ...
How did scientists do it and what have we learned since then? HD is a rare, adult-onset, autosomal dominant, progressive neurodegenerative disease. George Huntington (Figure 1) was the first ...
All in the Genes As Huntington’s is widely described as a hereditary disease, Dr Bhandari suggests, “HD is like a genetic puzzle ... While Huntington’s can affect people of any age ...
Roche’s drive to develop treatments for HD is inspired by the people whose lives are affected by this progressive and fatal inherited disease ... was nothing he could do other than to live ...
Kate is one of eight artists at the exhibition who have Huntington's disease. A group of people with the same "debilitating" disease have created a "joyful" art exhibition. Our Creative Journey ...
Qure's AMT-130 shows promising results for Huntington’s disease. Learn why QURE stock faces commercialization challenges ...
Mutant HTT drives Huntington's, and animal data suggest lowering levels of the protein could improve outcomes in a rare disease that causes people to gradually lose the ability to walk ...
The designation said that preliminary clinical data from the ongoing Phase 1/2 studies indicate AMT-130 has the potential to address unmet medical needs for the treatment of Huntington's disease.
An intellectually active lifestyle—in other words, the so-called cognitive reserve—has a protective effect on the progression and severity of the symptoms of motor, cognitive and psychiatric ...
Huntington’s is an inherited condition that is caused by a defect in a particular gene. This is responsible for making a protein which does not work properly in people ... s disease gene, I was told ...