Vertex Pharmaceuticals (NASDAQ:VRTX), a leading biotechnology company with a market capitalization of $113.7 billion, is navigating a critical juncture as it seeks to expand its therapeutic reach and ...

Genetic diseases caused by mutations in DNA, affect millions worldwide, leading to conditions ranging from cystic fibrosis to sickle ... employs cutting-edge gene editing technologies to ...

Discover the importance of vision, genetic eye disorders, and RNA-based therapies for precision treatment in India and ...

Fintel reports that on January 28, 2025, BTIG initiated coverage of Arcturus Therapeutics Holdings (NasdaqGM:ARCT) with a Buy ...

Casgevy, also known as exa-cel, was the first treatment to be licensed using gene-editing tool Crispr (Alamy/PA) A £1.65 million treatment has been approved for use for some NHS patients ...

In the new study, mice were created through genetic editing of mouse embryonic stem cells targeting a class of mammal-specific genes known as imprinted genes, of which there are about 200 ...

A research group led by Wei Li at the Chinese Academy of Sciences has created mice born from two male parents and capable of reaching adulthood. This builds on previous work from the group in ...

Children whose cystic fibrosis is caused by a rare gene variant are excluded from a new treatment which could potentially slow the decline in their lung function, it has emerged. A group of ...

NHS patients with sickle cell disease will be able to benefit from a groundbreaking gene-editing treatment that offers the prospect of a cure for the condition. The one-off gene therapy, known as ...