Medscape24d
Cystic Fibrosis Gene Therapy: Successes, Failures and Hopes for the Future
Uta Griesenbach, Eric W.F.W. Alton, Department of Gene Therapy, Faculty of Medicine ... proof-of-principle for gene transfer into the cystic fibrosis (CF) lung. It is currently unknown whether ...
Kaleido Scope6y
Gene Expression Core
Technically demanding protocols and reagents for cloning and propagating adenoviral and other recombinant viral systems, advances in gene suppression technology with sh- or siRNA, and capabilities for ...
Hosted on MSN1mon
ReCode to secure funds for cystic fibrosis gene correction treatments
ReCode Therapeutics is set to secure up to $15m in additional funding from the Cystic Fibrosis Foundation to enhance its gene correction ... ribonucleic acid (mRNA) therapy, currently in a Phase ...
pharmaphorum10y
Shire to develop mRNA technology with $15m cystic fibrosis collaboration
Shire is collaborating with Cystic Fibrosis Foundation Therapeutics (CFFT), the non-profit R&D arm of the Cystic Fibrosis Foundation, to support its Messenger RNA (mRNA) technology platform for CF.
Nature3y
Arcturus—a clinical-stage mRNA therapeutics and vaccines company
Arcturus’ lead clinical stage product candidates include a first-in-class, self-amplifying mRNA vaccine for COVID-19 and an mRNA replacement therapy ... for cystic fibrosis and influenza ...
Business Wire22d
Arcturus Therapeutics Announces Initiation of Dosing in Phase 2 Multiple Ascending Dose Studies for Cystic Fibrosis (CF) and Ornithine Transcarbamylase (OTC) Deficiency
“ARCT-810 is the only mRNA therapy ... Fibrosis Cystic fibrosis is a life-shortening disease with a worldwide prevalence. Mutations in the cystic fibrosis transmembrane conductance regulator ...