These engineered tRNAs have shown promise in restoring the function of proteins affected by nonsense mutations, particularly in the cystic fibrosis transmembrane conductance regulator (CFTR ...

While many are harmless, some are known to be involved in diseases, including cystic fibrosis ... 57% of missense mutations cause no harm, while around a third (32%) may be harmful, and the ...

In this review of RNA therapies, we paint an overview of what’s going on in a field that is addressing a number of diseases.

Patients aged 6 to 11 years with cystic fibrosis receiving 24-week once-daily vanzacaftor/tezacaftor/deutivacaftor generally ...

As harmful algal blooms (HABs) continue to spread across the globe, urgent research is needed to address this growing threat. Studies in Italy, China, and the Atlantic basin have shown that many ...

A class action lawsuit has been filed against Apple, alleging that some Apple Watch wristbands contain potentially hazardous levels of harmful chemicals. PFAS, also known as "forever chemicals ...

engages in developing and commercializing therapies for treating cystic fibrosis (CF). It markets TRIKAFTA/KAFTRIO for people with CF with at least one F508del mutation for 2 years of age or older ...

In the moment when her world shattered three years ago, Stephanie Mistre found her 15-year-old daughter, Marie, lifeless in the bedroom where she died by suicide. “I went from light to darkness ...

As we continue to explore the frontiers of genetics, correcting harmful mutations while simultaneously activating beneficial genes could lead to more effective treatments for various genetic ...

There are many misconceptions about CF. Learn the facts on our page, Dispelling Misconceptions About Cystic Fibrosis. In people with CF, mutations in the cystic fibrosis transmembrane conductance ...