Three people with a muscle-destroying disease destined to worsen got a little stronger when an implanted device zapped their ...

A new drug-free, minimally invasive intervention targets the root cause of progressive loss of neural function in spinal ...

From February 12, all newborn babies will be offered screening for spinal muscular atrophy (SMA), a rare progressive neuromuscular disease. SMA will be one of more than 20 other rare disorders ...

Edgewise Therapeutics , Inc. (NASDAQ:EWTX), with a market capitalization of $2.67 billion, is a biopharmaceutical company focused on developing innovative therapies for severe, rare muscle disorders.

PTC Therapeutics, Inc. (NASDAQ:PTCT), a biopharmaceutical company focused on developing and commercializing novel medicines for rare disorders, finds itself at a critical juncture. With a promising ...

Viatina-19, a Nelore cow from Brazil, was sold for a record $4 million, making her the world's most expensive cow. Renowned ...

The list of 36 drugs, which are exempt from basic customs duty, includes many expensive and imported medicines that can ...

The Muscular Dystrophy Association (MDA) is honoring a longtime researcher and an LGMD patient advocate with its 2025 Legacy ...

Discover the importance of vision, genetic eye disorders, and RNA-based therapies for precision treatment in India and ...