Kate Middleton joked about her “huge” hands as she left her print on the wall of the Ty Hafan children’s hospice in South ...

The Princess of Wales joined a music therapy session and was invited to add her handprint to the Ty Hafan children’s hospice ...

Diana helped to kickstart fundraising for the hospice in 1995, with Luciano Pavarotti performing a concert at Castle Castle to raise money for the charity at the Princess' request. Tŷ Hafan opened its ...

Scholar Rock submitted its BLA of apitegromab for the treatment of patients with Spinal Muscular Atrophy with a request for Priority Review to be given. Explore more details here.

Scholar Rock (SRRK), a late-stage biopharmaceutical company developing innovative treatments for spinal muscular atrophy, ...

Learn more about whether Ionis Pharmaceuticals, Inc. or PTC Therapeutics, Inc. is a better investment based on AAII's A+ Investor grades, which compare both companies' key financial metrics.

Problems with chemical messengers like dopamine were tied to posture issues in SMA in a mouse study, but levodopa therapy may ease symptoms.

Donald Trump continues to make waves in biopharma; Sage rejects Biogen’s unsolicited takeover offer; the obesity space sees ...

Life After, a documentary debuting today at Sundance, examines Elizabeth Bouvia's story, and conflicts between right-to-die ...

Filmmaker Reid Davenport weaves a powerful first-person perspective with a journalistic investigation about disability ...

More research is needed to confirm gray matter, the darker tissue found in the brain and spinal cord, “as a potential disease ...