Scholar Rock aims for a 2025 launch of apitegromab in SMA, expecting $2 billion in global revenue and significant growth from upcoming trials and favorable data.
Advocates rallied outside the State House on Tuesday for special education funding.The group urged lawmakers to allocate more ...
Crystal Rondeau’s muscle wasting disease has left her with only one finger to press an alarm button or send a text. The ...
Positive results from its Phase III STEER study mean Novartis could boost sales of its OAV101 IT drug for spinal muscular ...
Patients with spinal muscular atrophy (SMA) type 2 showed improved motor ability when treated with intrathecal onasemnogene ...
Known online as Squirmy and Grubs, YouTubers Hannah and Shane Burcaw have over 1.8 million subscribers. The married ...
Israel’s cabinet said yesterday that it was unlikely to meet to ratify a cease-fire agreement that had raised hopes for an ...
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According to the scientists of the National Research University "BelSU", the obtained results allow us to conclude that the ...
In a new essay collection, the influencer couple Shane and Hannah Burcaw peel back the layers of “interabled” relationships, ...
Creatinine, a byproduct of muscle function, may be more sensitive in tracking SMA progression and response to treatment than ...
While investors and analysts push for a deal, Biogen CEO Chris Viehbacher and Head of Development Priya Singhal refuse to ...
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