Did you see this? Nearly 1 in 10 Americans have asthma. Here's what causes it.

Sionna Therapeutics has closed its initial public offering, raising $191 million for its pipeline of therapies for cystic ...

In the 1980s, the discovery of the CFTR gene and mutations that cause CF further solidified the role of the sweat test in ...

Compare that with a disease like cystic fibrosis, which is caused by more than 2,000 mutations in what is known as the CFTR gene. “You can imagine, in theory, we could go and correct every ...

Despite new medication, cystic fibrosis often leads to permanent lung damage. Working with an international team, researchers ...

In their 2019 paper, Liu’s team used prime editing to alter the gene mutations causing sickle cell disease and Tay-Sachs disease. Liu explained that they attempted to edit mutated CFTR as well but ...

Limb-girdle muscular dystrophy type 2D (LGMD2D/R3) is a rare genetic disorder caused by mutations in the SGCA gene, leading to defective folding and the loss of functional α-sarcoglycan, with ...

For this, they used a mouse line that carries a mutation in the CFTR gene. Intravenous injections of SORT LNPs carrying a gene editor targeted to this mutation resulted in its correction in almost ...

CF is caused by mutations in the CF transmembrane conductance regulator (CFTR) gene, resulting in abnormal chloride and sodium transport across epithelial cells. While advancements like Trikafta ...