Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the ...

*Refers to the latest 2 years of omaha.com stories. Cancel anytime. A preview of Nebraska Medicine's Innovation Design Unit in December 2024 After more than four decades of infusing himself with ...

In the LIGHTHOUSE study, Atsena Therapeutics is evaluating ATSN-201 gene therapy for X-linked retinoschisis, leveraging AAV.SPR capsid for central retina transduction without foveal detachment risks.

genetic epilepsy, spinal muscular atrophy, hearing loss, cystic fibrosis, and "other severe and chronic diseases that are difficult to treat". The strategy aims to create an integrated national ...

Integrated gene therapy offers long-term relief for Haemophilia A Lentiviral vectors ensure safer treatment without immunosuppressants Clinical trial success boosts India’s global gene therapy ...

Cystic fibrosis, or CF, is a genetic disorder that causes the body ... but the condition can be treated with daily medications and therapy. "As I got older, [hockey] was actually kind of like ...

Cystic fibrosis, or CF, is a genetic disorder that causes the body to produce a ... but the condition can be treated with daily medications and therapy. "As I got older, [hockey] was actually kind of ...

Credit: Gorodenkoff via Shutterstock. US-based gene therapy startup, GEMMABio has raised $34m in seed funding to help advance its portfolio of gene therapy programmes. GEMMABio was founded by gene ...

The FDA has approved Vertex’s Alyftrek, a once-daily triple combination for the treatment of cystic fibrosis in people 6 years and older who have mutations that are amenable to the therapy ...

Vertex Pharmaceuticals said Friday the FDA has approved its next cystic fibrosis product ... is a triple-combination therapy intended for use in people with at least one F508del mutation or another ...

Cystic fibrosis (CF) is a genetic condition that leads to the production of thick, sticky mucus, which can cause complications in multiple organs, including the sinuses, lungs, intestines ...

Jaisalmer: India's indirect tax body has decided to exempt expensive cancer treatment gene therapy, penal charges levied by banks on loans, as well as rent paid by small businesses on property ...