Thirty patients have received the gene therapy within a clinical trial and early-access program, and the foundation also hopes to seek approval in the US.

Fate Therapeutics uses iPSC and gene editing to offer scalable off-the-shelf therapies. Read more to see why I rate FATE ...

Denali’s medicine and a similar one from Calico Life Sciences and AbbVie were not much different than a placebo, bringing the tally of failed drugs in the innovative “Healey platform trial” to seven.

In this manuscript, we give an overview of historical aspects, as well as the current state of clinical trials and approved gene therapy products for commercialization in Brazil. Focusing on gene ...

Gene therapy using modified blood stem cells helped five adults with severe hemophilia A reach therapeutic levels of clotting ...

Can You Get Netflix for Free in Other Ways? Although Netflix doesn't have a free trial directly, you can still technically get free Netflix through other means. The only true "free" option ...

Fast-track status will allow Solid Biosciences to have more frequent meetings with the FDA throughout the treatment-development process and, potentially, get the product to patients faster than would ...

Christopher Groux is an editor, writer and accessibility advocate. Before joining the Forbes Health team, he covered Accessibility at Reviewed and gaming at Inverse and Newsweek. When he’s not ...

He added that “in patients with hemophilia B in some of the earliest gene therapy trials now have pretty stable levels 10-12 years out. But this is one of the places where hemophilia A and B ...

Please provide your email address to receive an email when new articles are posted on . Percent-predicted FEV 1, sweat chloride and safety were analyzed in two phase 3 trials of vanzacaftor ...

9:00 a.m. The prosecution has rested is case in the trial of a grandmother who left a 7-month-old in a hot car. 8:56 a.m. The medical examiner said this was not “sudden death”. She said ...

"KATHERINE is a landmark clinical trial that found T-DM1 had such improved ... "From the excitement of identifying HER2 gene amplification and resultant protein overexpression as a targetable ...