Gene-editing kicked off 2024 with a bang in the medical sector but closed the year with a whimper. It started with the FDA ...

Introduction Cystic fibrosis (CF) is an autosomal recessive genetic disorder caused by mutations in the ... 38 We will use STATA 15.0 software to present the results and graphs of the NMA. When ...

Cystic fibrosis is a genetic condition that causes mucus in the body to become thick and sticky. The mucus throughout the body is typically slippery and acts as a protective barrier in the lungs ...

Researchers have developed a gene-editing treatment for prion disease that extends lifespan by about 50 percent in a mouse model of the fatal neurodegenerative condition. The treatment ...

The work has been reported in Nature Communications. SPLICER is a modification of the well known gene-editing technique known as CRISPR, in which a guide RNA takes a DNA-cutting enzyme called Cas9 to ...

The same is now possible in gene editing. Rather than employ separate tools for editing genes and regulating their expression, these distinct goals can now be combined into a single tool that can ...

Penn researchers introduce mvGPT, a gene editing tool that edits DNA, activates genes and represses gene expression simultaneously. Successfully tested on cells with Wilson’s disease, mvGPT addresses ...

A new genome editing tool—minimal versatile genetic perturbation technology (mvGPT)—can achieve simultaneous and orthogonal gene editing and gene regulation in human cells. The coming together ...