A Wicklow mother is among a concerned group of parents who are calling for individual trials of the modulator therapies for ...

Some people with cystic fibrosis still do not have access to the life-changing modulator therapy drugs, despite wider EMA ...

Vertex Pharmaceuticals Incorporated (NASDAQ:VRTX), with its substantial $114.5 billion market capitalization, continues to dominate the cystic fibrosis (CF) treatment market while advancing a ...

Sophie would make a world record for being the first man or woman with cystic fibrosis to row across the Atlantic, while at ...

The bottom line is few companies can match its combination of established leadership in rare diseases and realistic pathways ...

Vertex Pharmaceuticals Inc. (NASDAQ:VRTX), a leading biotechnology company specializing in cystic fibrosis (CF) treatments, has been making significant strides in expanding its therapeutic portfolio ...

FDA 2025 pulmonology drug alerts, including drug approvals/warnings, vaccine approvals, and medical device recalls/updates.

Orphan drugs offer critical treatment options for rare diseases, improving quality of life for underserved patients and ...

NHS England has agreed a deal with Vertex for its three-drug cystic fibrosis therapy Kaftrio ... who have two copies of the F508del mutation gene, or one copy of F508del and a minimal function ...

Vertex's lineup will look transformed in five years, and the company should continue performing well beyond that time. It's ...

Professor John Tregoning has spent the best part of the last two years testing longevity boosting theories to see if any work - his findings were surprising ...