Uta Griesenbach, Eric W.F.W. Alton, Department of Gene Therapy, Faculty of Medicine ... proof-of-principle for gene transfer into the cystic fibrosis (CF) lung. It is currently unknown whether ...
Technically demanding protocols and reagents for cloning and propagating adenoviral and other recombinant viral systems, advances in gene suppression technology with sh- or siRNA, and capabilities for ...
ReCode Therapeutics is set to secure up to $15m in additional funding from the Cystic Fibrosis Foundation to enhance its gene correction ... ribonucleic acid (mRNA) therapy, currently in a Phase ...
The gene correction program ... investigational inhaled mRNA therapy, which is currently enrolling a Phase 1b multi-dose study in people with CF. About Cystic Fibrosis Cystic fibrosis (CF) is ...
Sahay's lab studies lipid nanoparticles, or LNPs, as a gene delivery vehicle with a focus on cystic fibrosis, a progressive genetic disorder that results in persistent lung infection and affects ...
Arcturus’ lead clinical stage product candidates include a first-in-class, self-amplifying mRNA vaccine for COVID-19 and an mRNA replacement therapy ... for cystic fibrosis and influenza ...