Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the ...

*Refers to the latest 2 years of omaha.com stories. Cancel anytime. A preview of Nebraska Medicine's Innovation Design Unit in December 2024 After more than four decades of infusing himself with ...

Integrated gene therapy offers long-term relief for Haemophilia A Lentiviral vectors ensure safer treatment without immunosuppressants Clinical trial success boosts India’s global gene therapy ...

This novel therapy may be said to represent a quantum leap in targeted cancer treatments (1 Trusted Source This is not a regular anti-cancer vaccine, but an mRNA-based vaccine, the goal of ...

Courtesy of Gunnar Esiason There is no cure for cystic fibrosis, but the condition can be treated with daily medications and therapy. "As I got older, [hockey] was actually kind of like the ...

Credit: Gorodenkoff via Shutterstock. US-based gene therapy startup, GEMMABio has raised $34m in seed funding to help advance its portfolio of gene therapy programmes. GEMMABio was founded by gene ...

Vertex Pharmaceuticals VRTX announced that the FDA has approved its next-in-class vanza triple therapy for treating people with cystic fibrosis ... regulator (CFTR) gene responsive to the drug.

The technology-driven Nasdaq-100 has delivered an impressive performance in 2024, posting a nearly 30% return year-to-date. This strong showing has been propelled by a few standout stocks, while ...

Vertex Pharmaceuticals VRTX announced that the FDA has approved its next-in-class vanza triple therapy for treating people with cystic fibrosis (CF ... CF transmembrane conductance regulator (CFTR) ...

The FDA has approved Vertex’s Alyftrek, a once-daily triple combination for the treatment of cystic fibrosis in people 6 years and older who have mutations that are amenable to the therapy ...