The diagnosis of DMD was based on standard criteria: progressive symmetrical muscle weakness and other signs and symptoms starting before the age of 5 years; elevated serum creatinine kinase activity; ...

Contrary to prior data, this study shows that neither eosinophils nor STAT6-mediated IL-4/IL-13 signaling contribute ...

Lung biopsy is a relatively frequently performed procedure with considerable benefit for patient management but it may, on rare occasions, result in the death of the patient. It is a multidisciplinary ...

Sarepta’s gene therapy for Duchenne muscular dystrophy (DMD ... motor function in patients aged four to seven with the muscle-wasting disease. The gene therapy also failed a key efficacy ...

Vamorolone is a novel and fully synthetic glucocorticoid that has been shown in trials to slow down muscle degeneration and prolong the ability of DMD patients to walk without causing the weight ...

The musculoskeletal system is an organ system comprising the bones, muscles and connective tissues (including cartilage, tendons and ligaments) that bind tissues and organs together. The main ...