BioWorld2d
Ips Heart’s stem cell therapy designated orphan drug for Becker muscular dystrophy
Ips Heart Inc. has been awarded orphan drug designation by the FDA for its GIVI-MPC stem cell therapy for Becker muscular dystrophy. GIVI-MPC has the unique ability to create new muscle with full ...
The Miami Times2d
First female in the world receives revolutionary new gene therapy for muscular dystrophy in Miami
When Raniya Scott was just two years old, her world changed with an unexpected diagnosis: Duchenne muscular dystrophy (DMD), ...
Muscular Dystrophy News2d
My original diagnosis was incorrect. Here’s why that’s important.
Columnist Patrick Moeschen was given an incorrect diagnosis of Becker muscular dystrophy, years before learning he actually ...
Why Is Neuromuscular-Focused Dyne Therapeutics Stock Trading Lower On Friday?
Dyne Therapeutics' DYNE-101 shows promising Phase 1/2 results for myotonic dystrophy type 1, with plans for Accelerated ...
Dyne Therapeutics stock tumbles following trial data
Shares of Dyne Therapeutics, Inc. (Nasdaq: DYN) plummeted 25% as the biotechnology firm reported early trial data for its experimental therapy for myotonic dystrophy type 1 (DM1), a genetic disorder ...