While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...

The drugmaker sees additional growth opportunities in ophthalmology and neuromuscular disorders, Chief Medical Officer ...

MNDs are neurological disorders that destroy motor neurons, the cells that control skeletal muscle activity such as walking, breathing, speaking, and swallowing.

For this study, outcomes were compared between 2 groups of patients with myasthenia gravis: those who developed exacerbations ...

Hollywood actress Andie MacDowell shared that she's been diagnosed with a painful neuromuscular disorder called piriformis syndrome.

Application is supported by results from the DEVOTE study, which suggested that two doses of Spinraza (nusinerse) 50 mg taken ...

Andie MacDowell has revealed that she had been diagnosed with piriformis syndrome, a rare neuromuscular condition that ...

Biogen said the U.S. Food and Drug Administration has accepted its supplemental new-drug application, while the European Medicines Agency has validated its application, which confirms that the ...

Orphan drugs offer critical treatment options for rare diseases, improving quality of life for underserved patients and ...

"Men's gains in height and weight are more than double those of women's, increasing sexual size dimorphism," the researchers ...

NDAQ:SLDB) Solid Biosciences Receives FDA Fast Track Designation for SGT-212 Dual Route of Administration Gene Therapy for Friedreich's Ataxia ...

Dyne Therapeutics received fast-track designation from the Food and Drug Administration for a treatment of myotonic dystrophy type 1, a neuromuscular disease.