A Boston-area biopharmaceutical firm has submitted a biologics license application to the FDA for its investigational, fully ...

In surveys, parents of children with SMA and healthcare professionals in Sweden note the many ways the pandemic affected ...

A transformative initiative dedicated to enhancing lives through music launches at the Victoria Conservatory of Music in eponymous timing with an artist’s dream come true. The conservatory’s new ...

The list of 36 drugs, which are exempt from basic customs duty, includes many expensive and imported medicines that can ...

A case report described an infant with concurrent HDFN and SMA who was succesfully treated with an onasemnogene abeparvovec infusion.

Scholar Rock is asking the U.S. Food and Drug Administration to approve apitegromab for people with spinal muscular atrophy.

Scholar Rock submitted its BLA of apitegromab for the treatment of patients with Spinal Muscular Atrophy with a request for ...

Discover the importance of vision, genetic eye disorders, and RNA-based therapies for precision treatment in India and ...

The announcement was made at Arab Health 2025 where Sidra Medicine will highlight its international patient service programmes ...

KOCHI: Residents of Cherai are rallying to support two-and-a-half-year-old Adharv, who is suffering from Spinal Muscular ...