Creatinine, a byproduct of muscle function, may be more sensitive in tracking SMA progression and response to treatment than ...
Exercise can enhance the lives of people with spinal muscular atrophy ... our muscle weakness," said Michael Morale, who has SMA. "Now that many of us are on Spinraza or Evrysdi, ... many of our ...
Positive results from its Phase III STEER study mean Novartis could boost sales of its OAV101 IT drug for spinal muscular ...
Patients with spinal muscular atrophy (SMA) type 2 showed improved motor ability when treated with intrathecal onasemnogene ...