Investigators say adding RNA interference (RNAi) therapy to current treatment modalities may improve outcomes in patients ...
PH-894: Potent and Specific Silencing of BRD4 in NK CellsMarlborough, Massachusetts--( - October 16, 2024) - Phio ...
Wave Life Sciences' WVE-006 study shows significant promise in treating alpha-1 antitrypsin deficiency. Learn more about WVE ...
Vutrisiran treatment leads to a decrease in serum vitamin A levels. Supplementation of approximately, but not exceeding, 2500 IU to 3000 IU vitamin A per day is advised for patients taking vutrisiran.