More research is needed to confirm gray matter, the darker tissue found in the brain and spinal cord, “as a potential disease ...

Regulators in the U.S. and the European Union agreed to review Biogen’s applications for approval of a higher dose Spinraza ...

A woman with SMA type 3 became pregnant while on Spinraza treatment and gave birth to a healthy child, per a case report.

Columnist Alyssa Silva is recovering from a dangerous respiratory illness. With SMA, that means a whole lot more than it does ...

Nonadherence by SMA patients to their prescribed regimen of Evrysdi is linked to higher healthcare costs, a real-world U.S.

Creatinine, a byproduct of muscle function, may be more sensitive in tracking SMA progression and response to treatment than ...

As columnist Helen Baldwin continues to monitor her community's response to Hurricane Helene, she's seeing angel intervention ...

Human connections are fueled by many types of empathy, writes columnist Jasmine Ramos, who found some of that fuel from ...

I was familiar with the concept, but didn’t realize it was a common experience in the SMA community until a colleague brought it up. It goes like this: When boarding a flight, you calculate how much ...

A combination of a ready-to-use SMN protein and an experimental treatment targeting the SMN2 gene, which works in a similar way to Spinraza (nusinersen), eased abnormalities in motor neurons derived ...